GRANDRx is a new initiative that will catalyze the development of treatments for rare and neglected diseases. By implementing novel solutions throughout the research and healthcare system, it will transform the current “pipeline” into an integrated network. Established through the efforts of advocates, academia, industry, federal health agencies and other stakeholders, GRANDRx calls us to lend our expertise, our energy, and our voices towards a common goal. GRANDRx requires a culture shift within science, advocacy, and policy. All of these areas must move from focusing on single diseases and single issues, to focusing on commonalities, collaborations and system-wide change through an open and transparent process that will benefit all stakeholders. Just as with the Human Genome Project, open access to information, cross-disease focus, and transformed systems will lead to greater success. A substantial part of the effort will be dedicated to improving systems through sharing methodology leading to both successes and failures. Click Here for the GRANDRx Fact Sheet Join the Initiative Therapeutic development for rare and neglected diseases must step into the 21st century. This initiative is a coalition and is open to all stakeholders ready to collaborate and engage in system transformation.
